Rocket Pharmaceuticals

Rocket Pharmaceuticals

  • Founded: 2015
  • Location: Cranbury, NJ
  • Employee range: 50 - 200
  • Clinical stage: Clin2 (fast track)
  • Therapy area: Fanconi anemia (ODD)
  • Drug types: HEM, GEN, RAR, BON, IMM, CVV, MUS
  • Lead product: RP-L102
  • Product link: https://rocketpharma.com/our-disease-focus/
  • Funding: $100M stock Oct 2022; $6.5M grant Apr 2019; $78M stock Apr 2019


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Short description:

Gene Therapies

Drug notes:

RP-L201 Clin2 (fast track) leukocyte adhesion deficiency-1 (ODD); RP-A501 Clin1 (fast track) Danon disease (ODD); RP-L301 Clin1 (fast track) pyruvate kinase deficiency (ODD); RP-A601 Clin0 PKP2-ACM (ODD, FT); BAG3 RD cardiovascular

Long description:

Rocket Pharmaceuticals is a clinical-stage company developing gene therapy treatments for rare childhood disorders. Life-threatening childhood disorders such as Fanconi Anemia, Danon Disease and Leukocyte Adhesion Deficiency are caused by genetic mutations in single genes. Rocket is developing therapies that directly target these mutations in affected cell types using both adeno-associated viral vectors and lentiviral vectors. Rocket’s state-of-the-art laboratories are built for designing, optimizing and advancing candidate therapeutics to clinical stage development.

Jobs:

Rocket Pharmaceuticals
Coordinator, People Operations
Cranbury, NJ|3 days ago
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Rocket Pharmaceuticals
Senior Manager, QMS
Cranbury, NJ|7 days ago
Rocket Pharmaceuticals
Clinical Manufacturing Associate, Downstream
Cranbury, NJ|8 days ago
Rocket Pharmaceuticals
Director, Gene Therapy Regional Business Leader (G...
JE|21 days ago
Rocket Pharmaceuticals
Associate Director, Genetic Diagnostic Liaison- Ce...
JE|22 days ago
Rocket Pharmaceuticals
Manager, Environmental Health & Safety (EH&S)
Cranbury, NJ|28 days ago
Rocket Pharmaceuticals
Senior Manager, Apheresis Operations
Cranbury, NJ|36 days ago
Rocket Pharmaceuticals
Director, Statistical Programming
Cranbury, NJ|48 days ago
Rocket Pharmaceuticals
Clinical Trial Manager - Natural History
Cranbury, NJ|48 days ago
Rocket Pharmaceuticals
Director, Biostatistics - AAV
Cranbury, NJ|49 days ago
Rocket Pharmaceuticals
Director, Biostatistics - LVV
Cranbury, NJ|49 days ago
Rocket Pharmaceuticals
Director, Real-World Evidence
Cranbury, NJ|51 days ago
Rocket Pharmaceuticals
Senior Director, AAV Cardiovascular Marketing Lead...
Cranbury, NJ|62 days ago
Rocket Pharmaceuticals
Director, Information Technology - ePMO and Busine...
Cranbury, NJ|62 days ago
Rocket Pharmaceuticals
Manager, Metrology
Cranbury, NJ|66 days ago
Rocket Pharmaceuticals
Head of Business Excellence and Commercial Operati...
Cranbury, NJ|70 days ago
Rocket Pharmaceuticals
Sr. Lead Clinical Scientist, Hematology
Cranbury, NJ|72 days ago
Rocket Pharmaceuticals
Sr. Lead Clinical Scientist, Cardiovascular
Cranbury, NJ|72 days ago
Rocket Pharmaceuticals
Legal Contracts Manager
Cranbury, NJ|77 days ago
Rocket Pharmaceuticals
Manager, Information Technology - ERP Architecture...
Cranbury, NJ|79 days ago
Rocket Pharmaceuticals
Director, Information Technology - Commercial and ...
Cranbury, NJ|79 days ago
Rocket Pharmaceuticals
Vice President, Financial Planning & Analysis
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Director, Patient Advocacy
JE|100+ days ago
Rocket Pharmaceuticals
Associate Vice President, Head of Clinical Develop...
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Senior Medical Science Liaison- AAV (US, West Coas...
JE|100+ days ago
Rocket Pharmaceuticals
Senior Medical Science Liaison- AAV (US, East Coas...
JE|100+ days ago
Rocket Pharmaceuticals
Senior Medical Science Liaison- LVV (US, West Coas...
JE|100+ days ago
Rocket Pharmaceuticals
Senior Medical Science Liaison- LVV (US, East Coas...
JE|100+ days ago
Rocket Pharmaceuticals
Senior Medical Science Liaison- LVV (US, South)
JE|100+ days ago
Rocket Pharmaceuticals
Director, Global Regulatory Lead – LAD/PKD
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Director, Global Regulatory Lead – FA
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Associate Director, Regulatory Affairs (USL for AA...
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Manufacturing Supervisor, Downstream
Cranbury, NJ|100+ days ago


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