Short description:
Gene Therapies
Drug notes:
RP-L201 Clin2 (fast track) leukocyte adhesion deficiency-1 (ODD); RP-A501 Clin1 (fast track) Danon disease (ODD); RP-L301 Clin1 (fast track) pyruvate kinase deficiency (ODD); RP-A601 Clin0 PKP2-ACM (ODD, FT); BAG3 RD cardiovascular
Long description:
Rocket Pharmaceuticals is a clinical-stage company developing gene therapy treatments for rare childhood disorders. Life-threatening childhood disorders such as Fanconi Anemia, Danon Disease and Leukocyte Adhesion Deficiency are caused by genetic mutations in single genes. Rocket is developing therapies that directly target these mutations in affected cell types using both adeno-associated viral vectors and lentiviral vectors. Rocket’s state-of-the-art laboratories are built for designing, optimizing and advancing candidate therapeutics to clinical stage development.
Jobs:
Coordinator, People Operations Cranbury, NJ|3 days ago
Senior Manager, QMS Cranbury, NJ|7 days ago
Clinical Manufacturing Associate, Downstream Cranbury, NJ|8 days ago
Director, Gene Therapy Regional Business Leader (G... JE|21 days ago
Associate Director, Genetic Diagnostic Liaison- Ce... JE|22 days ago
Manager, Environmental Health & Safety (EH&S) Cranbury, NJ|28 days ago
Senior Manager, Apheresis Operations Cranbury, NJ|36 days ago
Director, Statistical Programming Cranbury, NJ|48 days ago
Clinical Trial Manager - Natural History Cranbury, NJ|48 days ago
Director, Biostatistics - AAV Cranbury, NJ|49 days ago
Director, Biostatistics - LVV Cranbury, NJ|49 days ago
Director, Real-World Evidence Cranbury, NJ|51 days ago
Senior Director, AAV Cardiovascular Marketing Lead... Cranbury, NJ|62 days ago
Director, Information Technology - ePMO and Busine... Cranbury, NJ|62 days ago
Manager, Metrology Cranbury, NJ|66 days ago
Head of Business Excellence and Commercial Operati... Cranbury, NJ|70 days ago
Sr. Lead Clinical Scientist, Hematology Cranbury, NJ|72 days ago
Sr. Lead Clinical Scientist, Cardiovascular Cranbury, NJ|72 days ago
Legal Contracts Manager Cranbury, NJ|77 days ago
Manager, Information Technology - ERP Architecture... Cranbury, NJ|79 days ago
Director, Information Technology - Commercial and ... Cranbury, NJ|79 days ago
Vice President, Financial Planning & Analysis Cranbury, NJ|100+ days ago
Director, Patient Advocacy JE|100+ days ago
Associate Vice President, Head of Clinical Develop... Cranbury, NJ|100+ days ago
Senior Medical Science Liaison- AAV (US, West Coas... JE|100+ days ago
Senior Medical Science Liaison- AAV (US, East Coas... JE|100+ days ago
Senior Medical Science Liaison- LVV (US, West Coas... JE|100+ days ago
Senior Medical Science Liaison- LVV (US, East Coas... JE|100+ days ago
Senior Medical Science Liaison- LVV (US, South) JE|100+ days ago
Director, Global Regulatory Lead – LAD/PKD Cranbury, NJ|100+ days ago
Director, Global Regulatory Lead – FA Cranbury, NJ|100+ days ago
Associate Director, Regulatory Affairs (USL for AA... Cranbury, NJ|100+ days ago
Manufacturing Supervisor, Downstream Cranbury, NJ|100+ days ago