Short description:
Gene Therapies
Drug notes:
RP-L201 Clin2 (fast track) leukocyte adhesion deficiency-1 (ODD); RP-A501 Clin1 (fast track) Danon disease (ODD); RP-L301 Clin1 (fast track) pyruvate kinase deficiency (ODD); RP-A601 Clin0 PKP2-ACM (ODD, FT); BAG3 RD cardiovascular
Long description:
Rocket Pharmaceuticals is a clinical-stage company developing gene therapy treatments for rare childhood disorders. Life-threatening childhood disorders such as Fanconi Anemia, Danon Disease and Leukocyte Adhesion Deficiency are caused by genetic mutations in single genes. Rocket is developing therapies that directly target these mutations in affected cell types using both adeno-associated viral vectors and lentiviral vectors. Rocket’s state-of-the-art laboratories are built for designing, optimizing and advancing candidate therapeutics to clinical stage development.
Jobs:
Clinical Manufacturing Associate I Cranbury, NJ|9 days ago
Senior Clinical Research Associate - US (East Coas... JE|19 days ago
Senior Clinical Research Associate - Netherlands JE|19 days ago
Senior Director, Financial Planning & R&D Finance Cranbury, NJ|24 days ago
Receptionist Cranbury, NJ|38 days ago
Lead, Lab Operations, Nonclinical R&D Cranbury, NJ|46 days ago
Senior Manager, Regulatory Affairs (EU) JE|47 days ago
Director, Regulatory Affairs - AAV Cranbury, NJ|47 days ago
Associate Director, Clinical Process Management & ... Cranbury, NJ|51 days ago
Manager, Field Reimbursement - West JE|54 days ago
Manager, Field Reimbursement - East JE|54 days ago
Director, Health Outcomes Cranbury, NJ|59 days ago
Director, Gene Therapy Regional Business Leader (G... JE|81 days ago
Director, Gene Therapy Regional Business Leader (G... JE|81 days ago
Associate Director, Technology Evaluation and Dili... Cranbury, NJ|85 days ago
Senior Manager, QMS Cranbury, NJ|87 days ago
Associate Director, Regulatory Operations Cranbury, NJ|92 days ago
Director, Biostatistics JE|99 days ago
Senior Lead Clinical Scientist, Cardiovascular Cranbury, NJ|100+ days ago
Senior Director, AAV Cardiovascular Marketing Lead... Cranbury, NJ|100+ days ago
Manager, Information Technology - ERP Architecture... Cranbury, NJ|100+ days ago