Rocket Pharmaceuticals

Rocket Pharmaceuticals

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  • Founded: 2015
  • Location: Cranbury, NJ
  • Employee range: 50 - 200
  • Clinical stage: Clin2 (fast track)
  • Therapy area: Fanconi anemia (ODD)
  • Drug types: HEM, GEN, RAR, BON, IMM, CVV, MUS
  • Lead product: RP-L102
  • Funding: $100M stock Oct 2022; $6.5M grant Apr 2019; $78M stock Apr 2019


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Business:

Gene Therapies

Drug notes:

RP-L201 Clin2 (fast track) leukocyte adhesion deficiency-1 (ODD); RP-A501 Clin1 (fast track) Danon disease (ODD); RP-L301 Clin1 (fast track) pyruvate kinase deficiency (ODD); RP-A601 Clin0 PKP2-ACM (ODD, FT); BAG3 RD cardiovascular

About:

Rocket Pharmaceuticals is a clinical-stage company developing gene therapy treatments for rare childhood disorders. Life-threatening childhood disorders such as Fanconi Anemia, Danon Disease and Leukocyte Adhesion Deficiency are caused by genetic mutations in single genes. Rocket is developing therapies that directly target these mutations in affected cell types using both adeno-associated viral vectors and lentiviral vectors. Rocket’s state-of-the-art laboratories are built for designing, optimizing and advancing candidate therapeutics to clinical stage development.

Rocket Pharmaceuticals
Scientist, Quality Control
Cranbury, NJ|1 day ago
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Rocket Pharmaceuticals
Scientist, Quality Control- Bioassay
Cranbury, NJ|1 day ago
Rocket Pharmaceuticals
Associate Vice President, Pharmacovigilance
Cranbury, NJ|4 days ago
Rocket Pharmaceuticals
Senior Associate Scientist- Quality Control
Cranbury, NJ|18 days ago
Rocket Pharmaceuticals
Senior Associate Scientist, Quality Control- Micro...
Cranbury, NJ|18 days ago
Rocket Pharmaceuticals
Director, Clinical Systems & TMF Operations
Cranbury, NJ|21 days ago
Rocket Pharmaceuticals
Manager, Quality Assurance
Cranbury, NJ|21 days ago
Rocket Pharmaceuticals
Manager, Quality Control- Stability
Cranbury, NJ|35 days ago
Rocket Pharmaceuticals
Summer Intern- Legal
Cranbury, NJ|36 days ago
Rocket Pharmaceuticals
Summer Intern- Business Excellence and Commercial ...
Cranbury, NJ|36 days ago
Rocket Pharmaceuticals
Summer Intern- Viral Vector Process Development, D...
Cranbury, NJ|37 days ago
Rocket Pharmaceuticals
Summer Intern- CMC Project Management
Cranbury, NJ|37 days ago
Rocket Pharmaceuticals
Summer Intern- Analytical Sciences and Cell Therap...
Cranbury, NJ|37 days ago
Rocket Pharmaceuticals
Summer Intern- Facilities Engineering
Cranbury, NJ|37 days ago
Rocket Pharmaceuticals
Senior Director, Scientific Communications
Cranbury, NJ|38 days ago
Rocket Pharmaceuticals
Senior Associate, Corporate Communications
Cranbury, NJ|42 days ago
Rocket Pharmaceuticals
Senior Accountant
New York City, NY|50 days ago
Rocket Pharmaceuticals
Associate Vice President, Quality Control
Cranbury, NJ|50 days ago
Rocket Pharmaceuticals
Director, Clinical Science Lead
Cranbury, NJ|63 days ago
Rocket Pharmaceuticals
Senior Manager, Investor Relations & Corporate Com...
JE|84 days ago
Rocket Pharmaceuticals
Director, Regulatory Affairs - AAV
Cranbury, NJ|94 days ago
Rocket Pharmaceuticals
Senior Director, Clinical Quality Assurance
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Director, Clinical Operations AAV
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Vice President, AAV Global Program Head
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Senior Director, Regulatory Advertising and Promot...
Cranbury, NJ|100+ days ago
Rocket Pharmaceuticals
Senior Director, Regulatory CMC (Chemistry, Manufa...
Cranbury, NJ|100+ days ago


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