Business:
Genetic Neuroscience Treatments
Drug notes:
Also Clin2 essential tremor; PRAX-562 Clin2 epilepsy; PRAX-628 Clin1 focal epilepsy; PRAX-222 Clin1 epilepsy; 6 programs Clin0 CNS disorders
About:
Praxis Precision Medicines is developing therapies for central nervous system (CNS) disorders by using insights from genetics. CNS disorders are characterized by neuronal excitation-inhibition imbalance. Praxis is using four key principles to increase the probability of success of finding therapies: [1] genetics to focus on targets identified through human genetics, [2] translational tools, to validate targets, [3] patient-guided development strategies and [4] efficient and rigorous clinical development paths. Praxis currently has two lead clinical programs for Epilepsy - CerebrumTM, a small molecule platform and SolidusTM, an antisense oligonucleotide platform.
Principal Scientist, Analytical DevelopmentPrincipal Scientist, Analytica... United States|4 days ago
Senior Manager, Analytical DevelopmentSenior Manager, Analytical Dev... United States|4 days ago
Senior Director, CMC Regulatory AffairsSenior Director, CMC Regulator... United States|6 days ago
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Executive Director, Process ChemistryExecutive Director, Process Ch... United States|6 days ago
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Commercial Lead, Movement DisordersCommercial Lead, Movement Diso... United States|13 days ago
Director, Clinical Quality - Program and Process Q...Director, Clinical Quality - P... United States|13 days ago
Program ExecutiveProgram Executive United States|16 days ago
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Clinical Operations LeadClinical Operations Lead Boston, MA|17 days ago
Clinical Research AssociateClinical Research Associate United States|18 days ago
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Director, Quantitative LeadDirector, Quantitative Lead United States|34 days ago
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Manager / Senior Manager Quality Management System...Manager / Senior Manager Quali... United States|37 days ago
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Portfolio Lead, Developmental Epileptic Encephalop...Portfolio Lead, Developmental ... United States|97 days ago
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