Short description:
Gene Therapy
Drug notes:
PBFT02 Clin1/Clin2 frontotemporal dementia; PBKR03 Clin1/Clin2 Krabbe disease; PBML04 Clin1/Clin2 metachromatic leukodystrophy; PBAL05 RD ALS; 2 undisclosed programs RD Huntington's disease, epilepsy
Long description:
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