Short description:
Antibody-Oligonucleotide Treatments for Muscle Diseases
Drug notes:
DYNE-251 Clin1/Clin2 DMD; DYNE-301 Clin0 facioscapulohumeral muscular dystrophy; 4 undisclosed programs RD/Clin0 DMD
Long description:
Dyne Therapeutics is developing therapeutics for patients living with muscle diseases with the aim of stopping or reversing disease progression. Many muscular diseases have a genetic underpinning: Dyne is using their proprietary FORCETM platform to develop targeted, modern oligonucleotide therapeutics to address these genetic defects and slow disease progression. Dyne’s therapeutics consist of an antibody to target the drug to the muscle, a payload that consists of either antisense oligonucleotides or short interfering RNAs to target the genetic basis of the disease, and linker to combine the two units. Dyne’s lead product candidate, DYNE-101 is currently anticipated for clinical trials for patients with Myotonic Dystrophy.
Jobs:
SVP, Head of Data Analytics Waltham, MA|4 days ago
Associate Director, Supply Chain Planning Waltham, MA|15 days ago
Neuromuscular Research Co-Op Waltham, MA|19 days ago
Research Data Sciences Co-Op Waltham, MA|19 days ago
Chief Information Officer Waltham, MA|19 days ago
Associate Director, Clinical Scientist Waltham, MA|22 days ago
VP, Global Market Access Waltham, MA|29 days ago
Associate Director, Statistical Programming Waltham, MA|33 days ago
Senior Scientist, Bioanalysis Waltham, MA|38 days ago
VP, Program Team Leader Waltham, MA|39 days ago
Director, Clinical Quality Assurance Waltham, MA|40 days ago
Executive Director, Medical Director Waltham, MA|52 days ago
SVP, Head of Clinical Development Waltham, MA|52 days ago
Director, Global Medical Affairs Lead Waltham, MA|52 days ago
Director, CMC Bioconjugation & External Manufactur... Waltham, MA|59 days ago
Senior Director, Drug Safety and Pharmacovigilance... Waltham, MA|59 days ago
SVP, Global Regulatory Affairs Waltham, MA|59 days ago
Senior Scientist, Oligonucleotide Chemistry Waltham, MA|73 days ago
Associate Director, Regulatory Operations Waltham, MA|73 days ago
Senior Director, Translational Biomarkers Waltham, MA|73 days ago
Vice President, Head of Compliance Waltham, MA|73 days ago
Director, Regulatory Affairs Waltham, MA|73 days ago
Senior Director, Clinical Pharmacology Waltham, MA|100+ days ago