Business:
Antibody-Oligonucleotide Treatments for Muscle Diseases
Drug notes:
DYNE-251 Clin1/Clin2 DMD; DYNE-301 Clin0 facioscapulohumeral muscular dystrophy; 4 undisclosed programs RD/Clin0 DMD
About:
Dyne Therapeutics is developing therapeutics for patients living with muscle diseases with the aim of stopping or reversing disease progression. Many muscular diseases have a genetic underpinning: Dyne is using their proprietary FORCETM platform to develop targeted, modern oligonucleotide therapeutics to address these genetic defects and slow disease progression. Dyne’s therapeutics consist of an antibody to target the drug to the muscle, a payload that consists of either antisense oligonucleotides or short interfering RNAs to target the genetic basis of the disease, and linker to combine the two units. Dyne’s lead product candidate, DYNE-101 is currently anticipated for clinical trials for patients with Myotonic Dystrophy.
Senior Manager, Clinical Supply Waltham, MA|16 days ago
Associate Director, Translational Biomarkers Waltham, MA|16 days ago
Associate Director, Clinical Operations Study Lead... Waltham, MA|23 days ago
Associate Director, Statistical Programming Waltham, MA|27 days ago
Principal Scientist, Bioinformatics Data Science Waltham, MA|31 days ago
Associate Director, CMC Biologics Waltham, MA|38 days ago
Associate Director, Oligonucleotide CMC and Extern... Waltham, MA|38 days ago
Director, Drug Product External Manufacturing Waltham, MA|38 days ago
Director, Regulatory Affairs CMC Waltham, MA|52 days ago
Associate Director, Clinical FP&A Waltham, MA|58 days ago
Associate Director, Biostatistics Waltham, MA|73 days ago
Senior Director, Quality Management System Waltham, MA|79 days ago
Senior Accountant Waltham, MA|86 days ago
Executive Director, EU Regulatory Affairs Waltham, MA|100+ days ago
Associate Director, Quantitative Pharmacology and ... Waltham, MA|100+ days ago
Director, Clinical Pharmacology and Pharmacometric... Waltham, MA|100+ days ago
VP, Program Team Leader Waltham, MA|100+ days ago
Director, Procurement Waltham, MA|100+ days ago
Director, Regulatory Affairs Waltham, MA|100+ days ago
Senior Director, Intellectual Property Senior Coun... Waltham, MA|100+ days ago
Senior Scientist, Bioanalysis Waltham, MA|100+ days ago
SVP, Head of Clinical Development Waltham, MA|100+ days ago