Business:
AAV Gene Therapy
Drug notes:
Undisclosed RD eye diseases
About:
Capsida Biotherapeutics is developing tissue-targeted, non-invasive gene therapies for rare and common diseases. Capsida’s approach is to use an intravenous delivery of a single, engineered capsid that can target individual or multiple organs simultaneously while limiting exposure to non-targeted organs. These capsids can deliver therapies that achieve gene replacement and gene editing and can therefore treat both monogenic and polygenic diseases. Capsida optimizes their capsids by using their automated, high-throughput biological screening method and is initially focused on targeting disorders of the central nervous system which have significant prevalence and unmet need.
Medical Director / Executive Medical Director, Cli... Thousand Oaks, CA|100+ days ago