Business:
Antibody-Oligonucleotide Conjugates
Drug notes:
AOC 1044 Clin1/Clin2 DMD (FT); AOC 1020 Clin1/Clin2 facioscapulohumeral muscular dystrophy; 3+ undisclosed programs RD DMD, skeletal muscle conditions, rare cardiac conditions
About:
Avidity Biosciences is developing a new class of RNA therapies to treat rare genetic diseases. Avidity has developed an innovative pipeline built upon their Antibody Oligonucleotide Conjugate (AOCTM) platform. AOCs comprise three components: monoclonal antibodies (mAbs), a linker and siRNA. AOCs therefore combine the specificity of mAbs and the precision of oligonucleotides which enable tissue-specific and gene-specific targeting, respectively. Avidity has primarily focused on skeletal muscle diseases with AOC 1001 now in clinical trials and is looking to expand into different cells and tissues. This can be achieved through the flexibility of the AOC platform.
Global Medical Director, FSHD CSS|1 day ago
Senior Manager, Cybersecurity CSS|4 days ago
Senior Manager, IT Infrastructure CSS|4 days ago
Associate Director, Clinical Operations CSS|5 days ago
Principle Clinical Research Associate CSS|5 days ago
Senior Research Associate, Bioanalytical CSS|6 days ago
Manager, IT Third-Party Risk CSS|6 days ago
Senior Clinical Trial Manager CSS|7 days ago
Associate Director, IT Development & Regulatory Bu... CSS|7 days ago
Supply Chain Shipping and Logistics Coordinator CSS|12 days ago
Quality Control Specialist (Raw Materials) CSS|12 days ago
Senior Clinical Trial Associate CSS|14 days ago
Staff Accountant CSS|19 days ago
Research Associate (oligonucleotide synthesis) CSS|19 days ago
Associate Director, Facilities CSS|19 days ago
National Account Director - Midwest/South Central CSS|20 days ago
National Account Director - Northeast CSS|20 days ago
National Account Director - Southeast CSS|20 days ago
National Account Director - West CSS|20 days ago
Associate Director, Regulatory Submissions Strateg... CSS|20 days ago
Manager, Clinical Supply Chain CSS|20 days ago
Senior Director, Clinical Development CSS|21 days ago
Associate Scientist CSS|22 days ago
Director, Research Data Science CSS|25 days ago
Senior Machine Learning Engineer CSS|25 days ago
Manager, Quality Control CSS|26 days ago
Research Associate CSS|32 days ago
Manager, Promotional Review Committee CSS|33 days ago
Executive Director, Corporate Communications CSS|36 days ago
Manager, Publications CSS|39 days ago
Senior Director, AOC (Oligo-linker) Process Develo... CSS|39 days ago
Medical Value Liaison, North America CSS|43 days ago
Senior Director, Field Medical Lead, North America... CSS|43 days ago
Director, Clinical Supply Chain CSS|61 days ago
Executive Director, Clinical Development CSS|100+ days ago