4D Molecular Therapeutics

4D Molecular Therapeutics

  • Founded: 2013
  • Location: Emeryville, CA
  • Employee range: 50 - 200
  • Clinical stage: Clin1/Clin2
  • Therapy area: Fabry disease
  • Drug types: GEN, OPH, RAR, LNG, GER, CVV
  • Lead product: 4D-310
  • Product link: https://4dmoleculartherapeutics.com/pipeline/
  • Funding: $138M stock May 2023; $222M IPO Dec 2020; $75M Jun 2020; $90M B Sep 2018; $20M prior


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Short description:

Gene Therapy

Drug notes:

4D-150 Clin1/Clin2 wet AMD, Clin0 DME; 4D-125 Clin1/Clin2 XLRP; 4D-110 Clin1/Clin2 choroideremia; 4D-710 Clin1/Clin2 cystic fibrosis, additional effort Clin0 cystic fibrosis; 4D-175 RD geographic atrophy; 4D-725 RD A1AT deficiency; undisclosed RD eye disease

Long description:

4D Molecular Therapeutics is designing and developing transformative gene therapies for unmet medical conditions. Adeno-associated viruses (AAVs) have great potential for targeted delivery and efficient transduction of gene therapies. 4D is using their Therapeutic Vector Evolution platform to discover custom and proprietary AAVs for specific tissues and diseases to build a diverse vector library. Selected vectors are chosen and tested in non-human primates based on their Target Vector Profile for a disease. Subsequent testing is performed in human cell and organotypic tissue assays. 4D is developing a diverse pipeline of product candidates for cardiology, pulmonology and ophthalmology with products in early clinical trials.

Jobs:

4D Molecular Therapeutics
Intern
Emeryville, CA|7 days ago
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4D Molecular Therapeutics
 Director, Corporate Counsel, Securities & Transac...
Emeryville, CA|21 days ago
4D Molecular Therapeutics
Sr. Scientist, Vector Innovation
Emeryville, CA|21 days ago
4D Molecular Therapeutics
Sr. Research Associate, Analytical Development & Q...
Emeryville, CA|25 days ago
4D Molecular Therapeutics
Medical Director, Ophtalmology
San Francisco, CA|34 days ago
4D Molecular Therapeutics
Research Associate II, Downstream
San Francisco, CA|43 days ago
4D Molecular Therapeutics
Research Associate
San Francisco, CA|62 days ago
4D Molecular Therapeutics
Sr. Director, Development Project Team Lead
Emeryville, CA|81 days ago
4D Molecular Therapeutics
Principal Scientist, Immunogenicity
Emeryville, CA|90 days ago
4D Molecular Therapeutics
Sr. Scientist, Potency Assays
Emeryville, CA|100+ days ago


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