Short description:
Gene Therapy
Drug notes:
4D-150 Clin1/Clin2 wet AMD, Clin0 DME; 4D-125 Clin1/Clin2 XLRP; 4D-110 Clin1/Clin2 choroideremia; 4D-710 Clin1/Clin2 cystic fibrosis, additional effort Clin0 cystic fibrosis; 4D-175 RD geographic atrophy; 4D-725 RD A1AT deficiency; undisclosed RD eye disease
Long description:
4D Molecular Therapeutics is designing and developing transformative gene therapies for unmet medical conditions. Adeno-associated viruses (AAVs) have great potential for targeted delivery and efficient transduction of gene therapies. 4D is using their Therapeutic Vector Evolution platform to discover custom and proprietary AAVs for specific tissues and diseases to build a diverse vector library. Selected vectors are chosen and tested in non-human primates based on their Target Vector Profile for a disease. Subsequent testing is performed in human cell and organotypic tissue assays. 4D is developing a diverse pipeline of product candidates for cardiology, pulmonology and ophthalmology with products in early clinical trials.
Jobs:
Principal Data Scientist - Statistical Programming... Emeryville, CA|4 days ago
Principal Data Scientist - Biostatistics Emeryville, CA|4 days ago
Scientist II Emeryville, CA|8 days ago
Clinical Records Associate, TMF Operations Emeryville, CA|9 days ago
Director, Clinical Science Emeryville, CA|16 days ago
Sr. Clinical Trial Associate Emeryville, CA|18 days ago
Scientist Emeryville, CA|19 days ago
Director, Clinical Quality Assurance (gene therapy... Emeryville, CA|24 days ago
Director, Clinical R&D Applications Emeryville, CA|33 days ago
Senior Manager, Competitive Intelligence Emeryville, CA|33 days ago
Associate Director, IT Compliance Emeryville, CA|43 days ago
Senior Scientist, Pharmacology Emeryville, CA|74 days ago
Sr. Research Associate, Potency Assays Emeryville, CA|78 days ago
Process Scientist II - Upstream Emeryville, CA|93 days ago
Scientist Emeryville, CA|94 days ago