Short description:
Gene Therapy
Drug notes:
4D-150 Clin1/Clin2 wet AMD, Clin0 DME; 4D-125 Clin1/Clin2 XLRP; 4D-110 Clin1/Clin2 choroideremia; 4D-710 Clin1/Clin2 cystic fibrosis, additional effort Clin0 cystic fibrosis; 4D-175 RD geographic atrophy; 4D-725 RD A1AT deficiency; undisclosed RD eye disease
Long description:
4D Molecular Therapeutics is designing and developing transformative gene therapies for unmet medical conditions. Adeno-associated viruses (AAVs) have great potential for targeted delivery and efficient transduction of gene therapies. 4D is using their Therapeutic Vector Evolution platform to discover custom and proprietary AAVs for specific tissues and diseases to build a diverse vector library. Selected vectors are chosen and tested in non-human primates based on their Target Vector Profile for a disease. Subsequent testing is performed in human cell and organotypic tissue assays. 4D is developing a diverse pipeline of product candidates for cardiology, pulmonology and ophthalmology with products in early clinical trials.
Jobs:
Associate Clinical Outsourcing & Business Ops Emeryville, CA|10 days ago
Senior Director, Data Management Emeryville, CA|12 days ago
QC Manager (External Testing), Analytical Developm... Emeryville, CA|16 days ago
Associate Director, Early-Stage Product Developmen... Emeryville, CA|16 days ago
Senior Scientist, Analytical Development and Quali... Emeryville, CA|16 days ago
Senior Data Manager - Clinical Data Emeryville, CA|18 days ago
Director, Data Science - Biostatistics Emeryville, CA|18 days ago
Manager, Regulatory Affairs - Document Control / V... Emeryville, CA|18 days ago
Scientist II Emeryville, CA|24 days ago
Medical Director Emeryville, CA|31 days ago
Senior Manager, CMC Project Management Emeryville, CA|31 days ago
Director, SEC Reporting and SOX Emeryville, CA|37 days ago
Scientist, Bioinformatics Emeryville, CA|40 days ago
Senior Medical Director - Ophthalmology Emeryville, CA|43 days ago
Sr. Manager, Quality Training Emeryville, CA|50 days ago
Associate Director, Regulatory Affairs Emeryville, CA|50 days ago
Principal Data Scientist - Statistical Programming... Emeryville, CA|50 days ago
Director, Biomarker & Immunology Emeryville, CA|53 days ago
Scientist II Emeryville, CA|58 days ago
Sr. HR Business Partner Emeryville, CA|60 days ago
Sr. Director, Program Management Emeryville, CA|71 days ago
Senior Director, Clinical Science (Remote) Remote|100+ days ago
Senior Scientist, Pharmacology Emeryville, CA|100+ days ago